Advancing the therapeutic potential of lentiviral β-globin gene therapy with selective decrease of α2-globin mRNA expression (#226)
Jim Vadolas
1
,
Tiwaporn Nualkaew
2
3
,
Brad McColl
2
,
Astrid Glaser
2
,
Suthat Fucharoen
3
,
Saovaros Svasti
3
,
Philippe Leboulch
4
5
,
Emmanuel Payen
5
6
- Centre of Cancer Research, Hudson Institute of Medical Research, Melbourne, VIC, Australia
- Cell and Gene Therapy Research group, Murdoch Childrens Research Institute, Royal Children’s Hospital, Parkville, VIC, Australia
- Thalassemia Research Center, Institute of Molecular Biosciences, Mahidol University, Nakhonpathom, Thailand
- Genetics Division, Brigham & Women’s Hospital and Harvard Medical School, Boston, MA, USA
- INSERM, Paris, France
- CEA François Jacob Biology Institute, Division of Innovative Therapies and UMR E007, University Paris-Saclay, Fontenay-aux-Roses, France
Publish consent withheld
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